# UNIVERSITY OF PENNSYLVANIA: IND-enabling studies of non-immunogenic gene therapy for ultra-rare DMD patients excluded from dystrophin trials

**Lab Budget Score:** 70/100

| Field | Value |
|---|---|
| Organization | UNIVERSITY OF PENNSYLVANIA |
| Location | PHILADELPHIA, PA |
| Project | IND-enabling studies of non-immunogenic gene therapy for ultra-rare DMD patients excluded from dystrophin trials |
| Project number | 5U01NS134672-03 |
| Mechanism | U01 |
| Institute | National Institute of Neurological Disorders and Stroke |
| Award | $2,792,126 |
| Awarded | 2026-09-03 |
| Project period | 2024-08-01 to 2027-07-31 |
| UEI | GM1XX56LEP58 |

## Why this score
- Award of $1M or more.
- Research or center grant: supplies, instruments and services budget.

Source: NIH RePORTER (newly awarded projects) (https://reporter.nih.gov/project-details/11408815). Last refreshed: 2026-11-04T21:37:56.465Z.
Award data comes from NIH RePORTER and may be revised by NIH. Organization-level only; investigator names and contacts are not included. Informational only.